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Molecular therapy. Nucleic acids
Published

CRISPR-Cas9-directed gene therapy for spinocerebellar ataxia type 1

Authors

Mihai Miclăuș, Gabriel Balmus

Abstract

Mol Ther Nucleic Acids. 2024 Nov 14;35(4):102377. doi: 10.1016/j.omtn.2024.102377. eCollection 2024 Dec 10.

NO ABSTRACT

PMID:39629115 | PMC:PMC11613173 | DOI:10.1016/j.omtn.2024.102377

UK DRI Authors

Gabriel Balmus

Prof Gabriel Balmus

Group Leader

Identifying genetic and environmental factors involved in DNA damage, neurodegeneration and ageing in neurons

Prof Gabriel Balmus